Supplementary Materials

The PDF file includes:

  • Fig. S1. Dose comparison with in utero enzyme replacement reveals higher tissue enzyme activity after 20 mg/kg compared to the 4 mg/kg dose.
  • Fig. S2. In utero enzyme replacement results in detectable enzyme in all tissues.
  • Fig. S3. Behavioral testing for open-field basic movement and rearing.
  • Fig. S4. Additional ELISA experiments.
  • Fig. S5. Peripheral blood chimerism and survival rates after IUHCT.
  • Fig. S6. Peripheral blood monocyte cross-correction.
  • Fig. S7. RNA sequencing studies and further data.

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Other Supplementary Material for this manuscript includes the following: