Supplementary Materials

The PDF file includes:

  • Materials and Methods
  • Fig. S1. Supplementary data for the dKO experiments.
  • Fig. S2. Supplementary data for the primate experiments.
  • Fig. S3. Proposed model of calpain 3 activation.
  • Table S1. Screening of primates for AAV9 seronegativity.
  • Table S2. Antibody response against the AAV9 serotype on sera (preimmune and sacrifice).
  • Table S3. Blood parameters of primates.
  • Table S4. Summary of echocardiogram analysis before and after systemic injection in primates.
  • References (4043)

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Other Supplementary Material for this manuscript includes the following:

  • Data file S1 (Microsoft Excel format). Individual subject-level data.