Supplementary Materials

The PDF file includes:

• Materials and Methods
• Fig. S1. Supplementary data for the dKO experiments.
• Fig. S2. Supplementary data for the primate experiments.
• Fig. S3. Proposed model of calpain 3 activation.
• Table S1. Screening of primates for AAV9 seronegativity.
• Table S2. Antibody response against the AAV9 serotype on sera (preimmune and sacrifice).
• Table S3. Blood parameters of primates.
• Table S4. Summary of echocardiogram analysis before and after systemic injection in primates.
• References (40–43)

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Other Supplementary Material for this manuscript includes the following:

• Data file S1 (Microsoft Excel format). Individual subject-level data.