Supplementary Materials
The PDF file includes:
- Materials and Methods
- Fig. S1. Supplementary data for the dKO experiments.
- Fig. S2. Supplementary data for the primate experiments.
- Fig. S3. Proposed model of calpain 3 activation.
- Table S1. Screening of primates for AAV9 seronegativity.
- Table S2. Antibody response against the AAV9 serotype on sera (preimmune and sacrifice).
- Table S3. Blood parameters of primates.
- Table S4. Summary of echocardiogram analysis before and after systemic injection in primates.
- References (40–43)
Other Supplementary Material for this manuscript includes the following:
- Data file S1 (Microsoft Excel format). Individual subject-level data.