Supplementary Materials

Supplementary Material for:

Hematopoietic Stem Cell Gene Therapy for Adenosine Deaminase–Deficient Severe Combined Immunodeficiency Leads to Long-Term Immunological Recovery and Metabolic Correctionta

H. Bobby Gaspar,* Samantha Cooray, Kimberly C. Gilmour, Kathryn L. Parsley, Fang Zhang, Stuart Adams, Emma Bjorkegren, Jinhua Bayford, Lucinda Brown, E. Graham Davies, Paul Veys, Lynette Fairbanks, Victoria Bordon, Theoni Petropolou, Christine Kinnon, Adrian J. Thrasher

*To whom correspondence should be addressed. E-mail: h.gaspar{at}

Published 24 August 2011, Sci. Transl. Med. 3, 97ra80 (2011)
DOI: 10.1126/scitranslmed.3002716

This PDF file includes:

  • Table S1. Follow-up of patients P3 and P5 who did not show a response to gene therapy and restarted ERT.
  • Table S2. Spectratype DkL values at last follow-up.
  • Fig. S1. CD4+ T cell spectratype histograms after gene therapy.

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