Article Information
vol. 9 no. 418
- Received for publication December 23, 2016
- Accepted for publication June 13, 2017
- .
Author Information
- Francesco Puzzo1,2,*,
- Pasqualina Colella1,*,
- Maria G. Biferi3,
- Deeksha Bali4,
- Nicole K. Paulk5,
- Patrice Vidal1,3,
- Fanny Collaud1,
- Marcelo Simon-Sola1,3,
- Severine Charles1,
- Romain Hardet3,
- Christian Leborgne1,
- Amine Meliani1,3,
- Mathilde Cohen-Tannoudji3,
- Stephanie Astord3,
- Bernard Gjata1,
- Pauline Sellier1,3,
- Laetitia van Wittenberghe1,
- Alban Vignaud1,
- Florence Boisgerault1,
- Martine Barkats3,
- Pascal Laforet6,
- Mark A. Kay5,
- Dwight D. Koeberl7,
- Giuseppe Ronzitti1,† and
- Federico Mingozzi1,3,†
- 1INTEGRARE, Genethon, Inserm, Univ Evry, Université Paris-Saclay, 91002 Evry, France.
- 2Department of Life Sciences and Biotechnology, University of Ferrara, Ferrara, Italy.
- 3University Pierre and Marie Curie Paris 6 and INSERM U974, Paris, France.
- 4Biochemical Genetics Laboratory, Duke University Health System, Durham, NC 27710, USA.
- 5Departments of Pediatrics and Genetics, Stanford University, Stanford, CA 94305, USA.
- 6Paris-Est Neuromuscular Center, Pitié-Salpêtrière Hospital and Raymond Poincaré Teaching Hospital, Garches, APHP, Paris, France.
- 7Division of Medical Genetics, Department of Pediatrics and Department of Molecular Genetics and Microbiology, Duke University School of Medicine, Durham, NC 27710, USA.
- ↵†Corresponding author. Email: gronzitti{at}genethon.fr (G.R.); fmingozzi{at}genethon.fr (F.M.)