FocusRegulatory Science

Protein Replacement Therapies for Rare Diseases: A Breeze for Regulatory Approval?

See allHide authors and affiliations

Science Translational Medicine  27 Mar 2013:
Vol. 5, Issue 178, pp. 178fs10
DOI: 10.1126/scitranslmed.3005007

Article Information

vol. 5 no. 178 178fs10

PubMed: 
Print ISSN: 
Online ISSN: 
History: 
  • .

Author Information

  1. Jennifer A. Gorzelany1,* and
  2. Mark P. de Souza2
  1. 1Laurelwood Biopartners, Boston, MA, 02115, USA.
  2. 2Lotus Tissue Repair, a wholly owned subsidiary of Shire Human Genetic Therapies, Lexington, MA 02421, USA.
  1. *Corresponding author. E-mail: jen{at}laurelwoodbio.com

Altmetric

Article usage

Article usage: March 2013 to August 2019

AbstractFullPdf
Mar 2013190078108
Apr 201317547383
May 20134812037
Jun 20134263645
Jul 20132681013
Aug 20132451722
Sep 20131942329
Oct 20131952244
Nov 20131222011
Dec 20131512226
Jan 20141031921
Feb 20141131326
Mar 20141072321
Apr 20141535131
May 2014123369
Jun 2014105208
Jul 2014432125
Aug 2014643230
Sep 2014512411
Oct 201444279
Nov 2014592315
Dec 2014532622
Jan 2015873138
Feb 2015512615
Mar 2015642720
Apr 2015621813
May 2015411212
Jun 2015511715
Jul 2015432112
Aug 201541106
Sep 201538640
Oct 20151858
Nov 2015301510
Dec 20151913
Jan 20162237
Feb 2016401719
Mar 2016702725
Apr 2016351822
May 2016531219
Jun 2016351322
Jul 2016261116
Aug 2016431026
Sep 2016631634
Oct 2016561230
Nov 2016551522
Dec 2016671950
Jan 2017512543
Feb 2017793250
Mar 2017612844
Apr 2017532039
May 2017522640
Jun 2017321924
Jul 2017431531
Aug 2017562033
Sep 2017681927
Oct 2017663137
Nov 2017562232
Dec 2017662232
Jan 2018602732
Feb 2018531948
Mar 2018532145
Apr 2018864973
May 20188321723
Jun 2018703247
Jul 2018413937
Aug 201839437
Sep 2018511948
Oct 2018216344
Nov 2018215341
Dec 2018912545
Jan 2019412040
Feb 20191311657
Mar 2019512845
Apr 2019145438
May 2019114621
Jun 2019104430
Jul 201961716
Aug 201952015

Navigate This Article