Research ArticleLysosomal Storage Diseases

Replacing the Enzyme α-l-Iduronidase at Birth Ameliorates Symptoms in the Brain and Periphery of Dogs with Mucopolysaccharidosis Type I

See allHide authors and affiliations

Science Translational Medicine  01 Dec 2010:
Vol. 2, Issue 60, pp. 60ra89
DOI: 10.1126/scitranslmed.3001380

Log in to view PDF

Log in through your institution

Log in through your institution

Stay Connected to Science Translational Medicine