eLetters is an online forum for ongoing peer review. Submission of eLetters are open to all. Please read our Terms of Service before submitting your own eLetter.
Research ArticleMuscular Dystrophy
A Naturally Occurring Human Minidysferlin Protein Repairs Sarcolemmal Lesions in a Mouse Model of Dysferlinopathy
- Martin Krahn1,2,*,
- Nicolas Wein1,*,
- Marc Bartoli1,3,*,
- William Lostal3,
- Sébastien Courrier1,
- Nathalie Bourg-Alibert3,
- Karine Nguyen1,2,
- Christophe Vial4,
- Nathalie Streichenberger5,
- Véronique Labelle2,
- Danielle DePetris1,
- Christophe Pécheux2,
- France Leturcq6,
- Pierre Cau1,
- Isabelle Richard3 and
- Nicolas Lévy1,2,†
- 1Inserm UMR_S 910, “Génétique Médicale et Génomique Fonctionnelle,” Faculté de Médecine de Marseille, Université de la Méditerranée, 13005 Marseille, France.
- 2Département de Génétique Médicale, Hôpital d’Enfants de la Timone, AP-HM, 13005 Marseille, France.
- 3Généthon, CNRS UMR8587 LAMBE, 91001 Evry, France.
- 4Hôpital neurologique Pierre Wertheimer, 69500 Lyon, France.
- 5Service de neuropathologie, hôpital neurologique, CHU de Lyon, 69500 Lyon, France.
- 6Laboratoire de Biochimie Génétique, Hôpital Cochin, AP-HP, 75014 Paris, France.
- ↵†To whom correspondence should be addressed. E-mail: nicolas.levy{at}univmed.fr
See allHide authors and affiliations
Science Translational Medicine 22 Sep 2010:
Vol. 2, Issue 50, pp. 50ra69
DOI: 10.1126/scitranslmed.3000951
Vol. 2, Issue 50, pp. 50ra69
DOI: 10.1126/scitranslmed.3000951
Martin Krahn
Nicolas Wein
Marc Bartoli
William Lostal
Sébastien Courrier
Nathalie Bourg-Alibert
Karine Nguyen
Christophe Vial
Nathalie Streichenberger
Véronique Labelle
Danielle DePetris
Christophe Pécheux
France Leturcq
Pierre Cau
Isabelle Richard
Nicolas Lévy
Submit a Response to This Article
No eLetters have been published for this article.