Research ArticleGene Therapy

Systemic AAV9.LAMP2B injection reverses metabolic and physiologic multiorgan dysfunction in a murine model of Danon disease

See allHide authors and affiliations

Science Translational Medicine  18 Mar 2020:
Vol. 12, Issue 535, eaax1744
DOI: 10.1126/scitranslmed.aax1744

Log in to view full text

Log in through your institution

Log in through your institution

Stay Connected to Science Translational Medicine

Navigate This Article