LetterDrug Discovery

Author Response to Comment on “Power of Rare Diseases: Found in Translation”

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Science Translational Medicine  19 Mar 2014:
Vol. 6, Issue 228, pp. 228lr1
DOI: 10.1126/scitranslmed.3008809

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The study of rare diseases in both academic and industry settings yields new knowledge about human pathophysiology and ultimately helps patients.

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