Research ArticleGene Therapy

Gene Therapy Prolongs Survival and Restores Function in Murine and Canine Models of Myotubular Myopathy

Science Translational Medicine  22 Jan 2014:
Vol. 6, Issue 220, pp. 220ra10
DOI: 10.1126/scitranslmed.3007523

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  1. Article
    1. Abstract
    2. INTRODUCTION
    3. RESULTS
    4. DISCUSSION
    5. MATERIALS AND METHODS
    6. SUPPLEMENTARY MATERIALS
    7. REFERENCES AND NOTES
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